Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

Virginia Tech researchers discovered an indication hidden in the brain that may help doctors identify children suffering from ...

Virginia Tech researchers have discovered an indication hidden in the brain that may help doctors identify children suffering ...

Experimental gene therapies like AMT‑130 lower toxic huntingtin protein and significantly slow Huntington’s disease, offering ...

A new CRISPR-based one-off procedure that lowers "bad" cholesterol has been approved to enter Phase I human trial. If ...

A new study confirms this long-held theory, discovering that 60 percent of defective genetic pairs impacting the production ...

Euan Ashley's lab explores the intricate interactions of gene variants. Tiny "typos," or genetic mutations, can sneak into ...

In an exciting scientific first, researchers at the Allen Institute successfully designed a new gene therapy that reversed symptoms related to SYNGAP1-related disorders (SRD) in mice. These are a ...

Genetic defects are exceedingly common, which is not surprising considering just how many cells make up our bodies, including our reproductive cells. While most of these defects have no or only minor ...

A protective APOE gene variant is enriched in Super Agers—people over 80 who think like 50‑year‑olds—cutting Alzheimer’s risk ...

Affecting 1 in 500 people, hypertrophic cardiomyopathy is a condition in which the walls of the left ventricle, the heart's main pumping chamber, become abnormally thick. "HCM is one of the primary ...

People often worry they will get Alzheimer’s disease if their parents did. But engaging in a healthy lifestyle can outweigh ...