Clinical and commercial quality controls are eased as the FDA looks to expedite therapy approvals in areas of unmet need.

Universal gene‑edited CAR‑T therapies turn donor T cells into off‑the‑shelf cancer treatments, cutting delays and costs while ...

The cell and gene therapy sector has never lacked attention, but all too often, the narrative swings from one extreme to ...

"Regulatory flexibility must be tailored for cell and gene therapies," commented FDA Commissioner Marty Makary. "These are ...

While GLP-1 (glucagon-like peptide-1) class obesity treatments like ‘Wegovy’ and ‘Mounjaro’ have gained immense popularity, ...

A "gene silencer" (technically known as small interfering RNA, or siRNA), locally delivered by nanoparticles embedded in an ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

The special properties of methylcellulose foam could make it a vehicle for bedside genetic engineering, according to a proof-of-principle study from bioengineers at Fred Hutch Cancer Center. In the ...

The government is using sickle cell treatments to test a new strategy: paying only if the therapies benefit patients. With ...

Key trends include strategic CDMO partnerships and a shift to in vivo administration, enhancing accessibility and innovation ...

What Is Waskyra, and Why Does It Matter? Waskyra (etuvetidigene autotemcel) is a new gene therapy approved to treat Wiskott-Aldrich syndrome (WAS), a rare inherited condition that affects the immune ...

A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain disorders known as SYNGAP1-related disorders, or SRDs. Researchers were able ...